Rare disease and real-world data: How RWD can help deliver better therapies and better outcomes

Planning a clinical trial for uncommon diseases is challenging due to small patient populations and knowledge gaps, which has a detrimental impact on the patient experience. In order to make more informed decisions and find new treatments for rare diseases, real-world data could be used to provide reliable proof and easier access to markets.

Read this report and you’ll understand:

  • The opportunities that RWD can bring in improving rare disease knowledge and treatments
  • Best practice to develop your own use of RWD to facilitate rare disease therapy solutions
  • How the industry is developing external partnerships to build the capabilities they need
  • What regulators expect from pharma and how regulatory pathways factor in
  • Outlining the best model approach for RWD 

Access this report now – to learn how RWD can help deliver improved patient-outcomes ->

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